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Recruitment and Apheresis Collection of Peripheral Blood Hematopoietic Stem Cells, Mononuclear Cells and Granulocytes
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 18 a 70 · Tout sèks · Mizajou Sep 22, 2026 · NCT00001405Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)
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7 Months – 15 Months · Tout sèks · Mizajou Aug 31, 2026 · NCT06805695Rett Syndrome Registry
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Laj 0 a 99 · Tout sèks · Mizajou Jun 30, 2026 · NCT05432349Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
Ap rekriteFaz 3
Laj 4 a 18 · Gason · Mizajou May 27, 2026 · NCT07608432To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome
Ap rekriteFaz 3
Laj 5 a 20 · Fanm · Mizajou Mar 27, 2026 · NCT06840496Sous ClinicalTrials.gov, done yo ranmase Oct 1, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.