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Uji klinis Talasemia Beta di Pennsylvania
5 studi untuk Talasemia Beta mencari peserta di lokasi di Pennsylvania.
Kota di Pennsylvania
Teks studi resmi (Bahasa Inggris)
ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia
- Children's Hospital of Philadelphia, Philadelphia
Menerima pesertaFase 1/2
Usia 18 hingga 40 · Semua jenis kelamin · Diperbarui 23 Sep 2026 · NCT06364774T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias
- Children's Hospital of Pittsburgh of UPMC, Pittsburgh
Menerima pesertaFase 1/2
Usia 5 hingga 40 · Semua jenis kelamin · Diperbarui 13 Agu 2026 · NCT03653338Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaStudi observasional
2 Months – 60 Years · Semua jenis kelamin · Diperbarui 13 Jan 2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaFase 2
2 Months – 55 Years · Semua jenis kelamin · Diperbarui 15 Des 2025 · NCT01962415A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel
- Children's Hospital of Philadelphia, Philadelphia
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 11 Feb 2025 · NCT06271512Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.