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Uji klinis Distrofi Otot Duchenne di Virginia

4 studi untuk Distrofi Otot Duchenne mencari peserta di lokasi di Virginia.

Kota di Virginia

Teks studi resmi (Bahasa Inggris)

A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

  • Children's Hospital of the King's Daughters, Norfolk
Menerima pesertaFase 3
Usia 7 hingga 11 · Pria · Diperbarui 28 Sep 2026 · NCT07160634

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

  • Children's Hospital of The King's Daughters, Norfolk
Menerima pesertaFase 1
Usia 2 ke atas · Pria · Diperbarui 11 Sep 2026 · NCT04626674

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

  • Children's Hospital of Richmond at VCU, Richmond
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 28 Jul 2026 · NCT07674758

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

  • Children's Hospital of the King's Daughters, Norfolk
Menerima pesertaFase 1/2
Usia 0 hingga 17 · Pria · Diperbarui 8 Jul 2026 · NCT06138639

Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.