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Uji klinis Penyakit Fabry di Pennsylvania

5 studi untuk Penyakit Fabry mencari peserta di lokasi di Pennsylvania.

Kota di Pennsylvania

Teks studi resmi (Bahasa Inggris)

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaFase 1/2
Usia 18 hingga 65 · Pria · Diperbarui 24 Sep 2026 · NCT06270316

A Study of Patients With Fabry Disease (US Specific)

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaStudi observasional
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 9 Sep 2026 · NCT06906367

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaFase 3
Usia 2 hingga 11 · Semua jenis kelamin · Diperbarui 1 Sep 2026 · NCT06904261

Fabry Disease Registry & Pregnancy Sub-registry

  • Geisinger Medical Center- Site Number : 840111, Danville
  • Penn State University Medical Center-Neurology- Site Number : 840104, Hershey
  • Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
  • dan 2 lainnya
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 23 Jun 2026 · NCT00196742

A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding

  • Amicus Therapeutics, Inc. Pregnancy Registry, Philadelphia
Menerima pesertaStudi observasional
Semua usia · Wanita · Diperbarui 8 Jul 2025 · NCT04252066

Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.