Beranda › Penyakit Fabry › Pennsylvania
Uji klinis Penyakit Fabry di Pennsylvania
5 studi untuk Penyakit Fabry mencari peserta di lokasi di Pennsylvania.
Kota di Pennsylvania
Teks studi resmi (Bahasa Inggris)
Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaFase 1/2
Usia 18 hingga 65 · Pria · Diperbarui 24 Sep 2026 · NCT06270316A Study of Patients With Fabry Disease (US Specific)
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaStudi observasional
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 9 Sep 2026 · NCT06906367A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaFase 3
Usia 2 hingga 11 · Semua jenis kelamin · Diperbarui 1 Sep 2026 · NCT06904261Fabry Disease Registry & Pregnancy Sub-registry
- Geisinger Medical Center- Site Number : 840111, Danville
- Penn State University Medical Center-Neurology- Site Number : 840104, Hershey
- Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
- dan 2 lainnya
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 23 Jun 2026 · NCT00196742A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding
- Amicus Therapeutics, Inc. Pregnancy Registry, Philadelphia
Menerima pesertaStudi observasional
Semua usia · Wanita · Diperbarui 8 Jul 2025 · NCT04252066Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.