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Uji klinis Penyakit Fabry di Virginia

6 studi untuk Penyakit Fabry mencari peserta di lokasi di Virginia.

Kota di Virginia

Teks studi resmi (Bahasa Inggris)

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • Lysosomal & Rare Disorders Research and Treatment Center, Inc, Fairfax
Menerima pesertaFase 1/2
Usia 18 hingga 65 · Pria · Diperbarui 24 Sep 2026 · NCT06270316

A Study of Patients With Fabry Disease (US Specific)

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
Menerima pesertaStudi observasional
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 9 Sep 2026 · NCT06906367

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
Menerima pesertaFase 3
Usia 2 hingga 11 · Semua jenis kelamin · Diperbarui 1 Sep 2026 · NCT06904261

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease

  • Lysosomal and Rare Disorders Research and Treatment Center Inc, Fairfax
Menerima pesertaFase 2/3
Usia 2 hingga 17 · Semua jenis kelamin · Diperbarui 10 Agu 2026 · NCT06328608

Fabry Disease Registry & Pregnancy Sub-registry

  • O & O Alpan- Site Number : 840025, Fairfax
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 23 Jun 2026 · NCT00196742

A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients

  • Lysosomal & Rare Disorder Research & Treatment Center (LRDRTC), Fairfax
Menerima pesertaStudi observasional
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 14 Nov 2025 · NCT06663358

Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.