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Uji klinis Penyakit Gaucher di Pennsylvania

5 studi untuk Penyakit Gaucher mencari peserta di lokasi di Pennsylvania.

Kota di Pennsylvania

Teks studi resmi (Bahasa Inggris)

A Gaucher Disease Gene Therapy Trial With FLT201

  • Children's Hospital of Philadelphia, Philadelphia
  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaFase 3
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 3 Sep 2026 · NCT07223944

International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

  • Penn State Health Milton South Hershey Medical Center- Site Number : 840126, Hershey
  • Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
  • Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
  • dan 1 lainnya
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 14 Apr 2026 · NCT00358943

Longitudinal Study of Neurodegenerative Disorders

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 9 Feb 2026 · NCT03333200

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaStudi observasional
2 Months – 60 Years · Semua jenis kelamin · Diperbarui 13 Jan 2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaFase 2
2 Months – 55 Years · Semua jenis kelamin · Diperbarui 15 Des 2025 · NCT01962415

Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.