Beranda › Penyakit Gaucher › Pennsylvania
Uji klinis Penyakit Gaucher di Pennsylvania
5 studi untuk Penyakit Gaucher mencari peserta di lokasi di Pennsylvania.
Kota di Pennsylvania
Teks studi resmi (Bahasa Inggris)
A Gaucher Disease Gene Therapy Trial With FLT201
- Children's Hospital of Philadelphia, Philadelphia
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaFase 3
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 3 Sep 2026 · NCT07223944International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry
- Penn State Health Milton South Hershey Medical Center- Site Number : 840126, Hershey
- Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
- Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
- dan 1 lainnya
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 14 Apr 2026 · NCT00358943Longitudinal Study of Neurodegenerative Disorders
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 9 Feb 2026 · NCT03333200Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaStudi observasional
2 Months – 60 Years · Semua jenis kelamin · Diperbarui 13 Jan 2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaFase 2
2 Months – 55 Years · Semua jenis kelamin · Diperbarui 15 Des 2025 · NCT01962415Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.