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Beranda › Kelainan Genetik › New York

Uji klinis Kelainan Genetik di New York

7 studi untuk Kelainan Genetik mencari peserta di lokasi di New York.

Kota di New York

Teks studi resmi (Bahasa Inggris)

Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)

  • Icahn School of Medicine at Mount Sinai, New York
Menerima pesertaStudi observasional
7 Months – 15 Months · Semua jenis kelamin · Diperbarui 31 Agu 2026 · NCT06805695

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)

  • Jacobi Medical Center, The Bronx
Menerima pesertaFase 2
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 5 Agu 2026 · NCT07224360

Helix Research Network

  • Rochester Regional Health (GenoWell), Rochester
Menerima pesertaStudi observasionalSukarelawan sehat diterima
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 23 Mar 2026 · NCT06057181

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • Icahn School of Medicine at Mount Sinai, New York
Menerima pesertaFase 1/2
Usia 1 ke atas · Semua jenis kelamin · Diperbarui 23 Mar 2026 · NCT05130437

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

  • New York Presbyterian Hospital - Morgan Stanley Children's Hospital, New York
Menerima pesertaFase 3
Usia 12 hingga 35 · Semua jenis kelamin · Diperbarui 23 Mar 2026 · NCT05477563

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Icahn School of Medicine at Mount Sinai - Clinical Research Unit, New York
Menerima pesertaFase 1/2
Semua usia · Semua jenis kelamin · Diperbarui 22 Jan 2026 · NCT04159103

STXBP1 and SYNGAP1 Related Disorders Natural History Study

  • Weill Cornell Medicine, New York
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 29 Okt 2025 · NCT06555965

Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.