Beranda › Kelainan Genetik › North Carolina
Uji klinis Kelainan Genetik di North Carolina
9 studi untuk Kelainan Genetik mencari peserta di lokasi di North Carolina.
Kota di North Carolina
Teks studi resmi (Bahasa Inggris)
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- Duke University Health System, Durham
Menerima pesertaStudi observasionalSukarelawan sehat diterima
1 Month – 100 Years · Semua jenis kelamin · Diperbarui 2 Okt 2026 · NCT02450851Inherited Reproductive Disorders
- NIEHS Clinical Research Unit (CRU), Research Triangle Park
Menerima pesertaStudi observasional
6 Weeks – 120 Years · Semua jenis kelamin · Diperbarui 28 Jul 2026 · NCT01500447Rett Syndrome Registry
- The University of North Carolina at Chapel Hill, Chapel Hill
Menerima pesertaStudi observasional
Usia 0 hingga 99 · Semua jenis kelamin · Diperbarui 30 Jun 2026 · NCT05432349Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
- Rare Disease Research, LLC, Hillsborough
Menerima pesertaFase 3
Usia 4 hingga 18 · Pria · Diperbarui 27 Mei 2026 · NCT07608432Helix Research Network
- Cone Health (Gene Connect), Burlington
- WakeMed (PreciselyYou), Raleigh
Menerima pesertaStudi observasionalSukarelawan sehat diterima
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 23 Mar 2026 · NCT06057181A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
- Duke University Medical System (Duke Health), Durham
Menerima pesertaFase 1/2
Usia 1 ke atas · Semua jenis kelamin · Diperbarui 23 Mar 2026 · NCT05130437Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease
- Levine Children's Hospital - Hematology, Charlotte
Menerima pesertaFase 3
Usia 12 hingga 35 · Semua jenis kelamin · Diperbarui 23 Mar 2026 · NCT05477563PKP2-ACM Natural History Study
- Duke University, Durham
Menerima pesertaStudi observasional
Usia 12 ke atas · Semua jenis kelamin · Diperbarui 27 Feb 2026 · NCT06644742Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- Duke University Medical System (Duke Health), Durham
Menerima pesertaFase 1/2
Semua usia · Semua jenis kelamin · Diperbarui 22 Jan 2026 · NCT04159103Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.