Beranda › Penyakit Penyimpanan Glikogen Tipe II › California
Uji klinis Penyakit Penyimpanan Glikogen Tipe II di California
5 studi untuk Penyakit Penyimpanan Glikogen Tipe II mencari peserta di lokasi di California.
Kota di California
Teks studi resmi (Bahasa Inggris)
A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease
- University of California-Irvine, Irvine
Menerima pesertaFase 1
Usia 18 hingga 75 · Semua jenis kelamin · Diperbarui 17 Agu 2026 · NCT07354724A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
- University of California, Irvine (UCI), Irvine
- Stanford Neuroscience Health Center, Palo Alto
Menerima pesertaFase 1/2
Usia 18 hingga 65 · Semua jenis kelamin · Diperbarui 20 Jul 2026 · NCT07282847Pompe Disease Registry Protocol
- University of California at Irvine- Site Number : 840036, Irvine
- Southern California Permanente Medical Group- Site Number : 840108, Los Angeles
- Children's Hospital of Orange County- Site Number : 840074, Orange
- dan 3 lainnya
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 23 Jun 2026 · NCT00231400Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- University of California - Irvine Medical Center, Irvine
Menerima pesertaFase 2
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 23 Jun 2026 · NCT07123155A Global Prospective Observational Registry of Patients With Pompe Disease
- University of California Irvine, Irvine
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 10 Mar 2026 · NCT06121011Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.