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Uji klinis Penyakit Penyimpanan Glikogen Tipe II di North Carolina

8 studi untuk Penyakit Penyimpanan Glikogen Tipe II mencari peserta di lokasi di North Carolina.

Kota di North Carolina

Teks studi resmi (Bahasa Inggris)

A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease

  • Duke University School of Medicine - Early Phase Research Unit, Durham
Menerima pesertaFase 1
Usia 18 hingga 75 · Semua jenis kelamin · Diperbarui 17 Agu 2026 · NCT07354724

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

  • Duke University, Durham
Menerima pesertaFase 1/2
Usia 18 hingga 65 · Semua jenis kelamin · Diperbarui 20 Jul 2026 · NCT07282847

Pompe Disease Registry Protocol

  • Carolinas Medical Center Hospital- Site Number : 840065, Charlotte
  • Duke University Medical Center Genetics Dept- Site Number : 840037, Durham
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 23 Jun 2026 · NCT00231400

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Duke University Medical Center, Durham
Menerima pesertaFase 2
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 23 Jun 2026 · NCT07123155

Pompe Pregnancy Sub-Registry

  • Duke University Medical Center Genetics Dept- Site Number : 840037, Durham
Menerima pesertaStudi observasional
Semua usia · Wanita · Diperbarui 16 Apr 2026 · NCT00567073

Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease

  • Duke University Medical Center, Durham
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 8 Apr 2026 · NCT01665326

A Global Prospective Observational Registry of Patients With Pompe Disease

  • Duke University Medical Center, Durham
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 10 Mar 2026 · NCT06121011

Cognitive and Neurological Pathologies in Pompe Disease

  • Duke University Medical Center, Durham
Menerima pesertaStudi observasional
Usia 0 hingga 18 · Semua jenis kelamin · Diperbarui 4 Mar 2026 · NCT04639336

Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.