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Uji klinis Hemofilia B di California

7 studi untuk Hemofilia B mencari peserta di lokasi di California.

Kota di California

Teks studi resmi (Bahasa Inggris)

Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

  • The Regents of the University of California||UC Davis Health, Rancho Cordova
  • UC Davis Health, Sacramento
  • UC Davis Ambulatory Care Clinic, Sacramento
  • dan 3 lainnya
Menerima pesertaFase 3
Usia 18 ke atas · Pria · Diperbarui 2 Okt 2026 · NCT05568719

Phase 3, Open-label, Single-dose Study of CSL222 in Adolescent Male Subjects (≥ 12 to < 18 Years of Age) With Severe or Moderately Severe Hemophilia B

  • Center for Inherited Blood Disorders, Orange
Menerima pesertaFase 3
138 Months – 206 Months · Pria · Diperbarui 16 Sep 2026 · NCT07080905

A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B

  • Orthopaedic Hemophilia Treatment Center, Los Angeles
  • David Geffen School of Medicine at UCLA, Los Angeles
  • Children's Hospital Los Angeles, Los Angeles
  • dan 2 lainnya
Menerima pesertaFase 1/2
Usia 2 ke atas · Pria · Diperbarui 11 Sep 2026 · NCT06379789

Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs)

  • University of California, San Diego (UCSD), San Diego
Menerima pesertaFase 3
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 27 Agu 2026 · NCT06003387

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Orthopaedic Institute for Children HTC, Los Angeles
  • Childrens Hospital Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital Oakland, Oakland
  • dan 5 lainnya
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 17 Agu 2026 · NCT04398628

A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)

  • Children's Hospital Los Angeles, Los Angeles
Menerima pesertaFase 1Sukarelawan sehat diterima
Usia 18 hingga 60 · Semua jenis kelamin · Diperbarui 2 Jul 2026 · NCT06349473

SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors

  • Orthopaedic Institute for Children, Los Angeles
  • University of California at Davis UC Davis Hemostasis and Thrombosis Center, Sacramento
Menerima pesertaFase 4
Usia 12 hingga 100 · Semua jenis kelamin · Diperbarui 12 Jan 2026 · NCT04647227

Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.