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Uji klinis Hemofilia B di Philadelphia, PA

5 studi untuk Hemofilia B mencari peserta di lokasi sekitar Philadelphia (dalam radius sekitar 30 mil). Buka studi untuk melihat kriteria peserta dan cara menghubungi tim studi.

Teks studi resmi (Bahasa Inggris)

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Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

Menerima pesertaFase 3
  • The Childrens Hospital of Philadelphia Division of Hematology, Philadelphia
  • The Childrens Hospital of Philadelphia Division of Hematology, Philadelphia
Usia 18 ke atas · Pria · Diperbarui 2 Okt 2026 · NCT05568719

A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B

Menerima pesertaFase 1/2
  • Children's Hospital of Philadelphia (CHOP), Philadelphia
Usia 2 ke atas · Pria · Diperbarui 11 Sep 2026 · NCT06379789

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

Menerima pesertaStudi observasional
  • Children's Hospital of Philadelphia, Philadelphia
  • Penn Comprehensive Hemophilia and Thrombophilia Program/Hospital of the University of Pennsylvania, Philadelphia
  • St. Christopher's Hospital for Children, Philadelphia
  • dan 1 lainnya
Semua usia · Semua jenis kelamin · Diperbarui 17 Agu 2026 · NCT04398628

A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)

Menerima pesertaFase 1Sukarelawan sehat diterima
  • Perelman Center for Advanced Medicine (PCAM)- Penn Blood Disorders Program, Philadelphia
Usia 18 hingga 60 · Semua jenis kelamin · Diperbarui 2 Jul 2026 · NCT06349473

Open-Label Extension Study of Marstacimab in Hemophilia Participants With or Without Inhibitors

Menerima pesertaFase 3
  • The Feinstein Institutes for Medical Research, Philadelphia
Usia 1 hingga 74 · Pria · Diperbarui 1 Jul 2026 · NCT05145127

Uji klinis Hemofilia B di kota lain

Studi lain di Philadelphia

Dari ClinicalTrials.gov, data diambil 6 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.