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Uji klinis Hemofilia di California

14 studi untuk Hemofilia mencari peserta di lokasi di California.

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Teks studi resmi (Bahasa Inggris)

Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

  • The Regents of the University of California||UC Davis Health, Rancho Cordova
  • UC Davis Health, Sacramento
  • UC Davis Ambulatory Care Clinic, Sacramento
  • dan 3 lainnya
Menerima pesertaFase 3
Usia 18 ke atas · Pria · Diperbarui 2 Okt 2026 · NCT05568719

A Study to Test a Medicine (Fitusiran) for Preventing Bleeds in People With Severe Hemophilia Who Previously Received Preventive Treatment With Emicizumab

  • Children's Hospital Los Angeles- Site Number : 8400005, Los Angeles
Menerima pesertaFase 4
Usia 12 ke atas · Pria · Diperbarui 23 Sep 2026 · NCT06145373

A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of NXT007 in Persons With Severe or Moderate Hemophilia A

  • UC Davis Cancer Center, Sacramento
Menerima pesertaFase 1/2
Usia 2 hingga 59 · Pria · Diperbarui 11 Sep 2026 · NCT05987449

A Gene Therapy Study of SPK-8011QQ in Adults With Severe or Moderately Severe Hemophilia A

  • Center for Inherited Blood Disorders, Orange
  • University of California San Francisco, San Francisco
  • Kaiser Permanente, Vallejo
Menerima pesertaFase 1/2
Usia 18 ke atas · Pria · Diperbarui 11 Sep 2026 · NCT07226206

A Clinical Study to Evaluate the Effects of NXT007 Compared to Emicizumab Prophylaxis in People With Hemophilia A

  • Center for Inherited Blood Disorders, Orange
Menerima pesertaFase 3
Usia 12 ke atas · Semua jenis kelamin · Diperbarui 4 Sep 2026 · NCT07416604

Pharmacokinetics, Pharmacodynamics, and Safety Profile of Understudied Drugs Administered to Children Per Standard of Care (POPS)

  • Lucile Packard Children's Hospital, Palo Alto
Menerima pesertaStudi observasionalSukarelawan sehat diterima
Usia 0 hingga 20 · Semua jenis kelamin · Diperbarui 21 Agu 2026 · NCT04278404

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Orthopaedic Institute for Children HTC, Los Angeles
  • Childrens Hospital Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital Oakland, Oakland
  • dan 5 lainnya
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 17 Agu 2026 · NCT04398628

A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B

  • The Luskin Orthopaedic Institute for Children- Site Number : 8400013, Los Angeles
  • The Center for Inherited Blood Disorders- Site Number : 8400009, Orange
Menerima pesertaFase 3
Usia 1 hingga 11 · Pria · Diperbarui 17 Agu 2026 · NCT07285460

Prevention of Bleeding in Patients With Moderate and Severe Hemophilia A Playing Sports: A Comparison Between Factor VIII and Emicizumab Prophylaxis

  • Stanford University, Palo Alto
  • Rady Children's Hospital, San Diego
Menerima pesertaStudi observasional
Usia 6 hingga 19 · Semua jenis kelamin · Diperbarui 2 Jul 2026 · NCT05022459

A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)

  • Children's Hospital Los Angeles, Los Angeles
Menerima pesertaFase 1Sukarelawan sehat diterima
Usia 18 hingga 60 · Semua jenis kelamin · Diperbarui 2 Jul 2026 · NCT06349473

A Study to Learn About How Changing Therapy From Emicizumab to Marstacimab Affects People With the Severe Hemophilia A.

  • Orthopaedic Institute for Children/Orthopaedic Hemophilia Treatment Center, Los Angeles
Menerima pesertaFase 1
Usia 12 hingga 74 · Pria · Diperbarui 3 Jun 2026 · NCT06703606

Emicizumab for Severe Von Willebrand Disease (VWD) and VWD/Hemophilia A

  • The Center for Comprehensive Care and Diagnosis of Inherited Blood Disorders (CIBD), Orange
  • Stanford University: Stanford Children's Health, Redwood City
Menerima pesertaFase 1
Usia 0 hingga 90 · Semua jenis kelamin · Diperbarui 3 Apr 2026 · NCT05500807

SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors

  • Orthopaedic Institute for Children, Los Angeles
  • University of California at Davis UC Davis Hemostasis and Thrombosis Center, Sacramento
Menerima pesertaFase 4
Usia 12 hingga 100 · Semua jenis kelamin · Diperbarui 12 Jan 2026 · NCT04647227

Efanesoctocog Alfa Prophylaxis in Patients With Hemophilia A With Synovial Hypertrophy

  • Orthopedic Institute for Children- Site Number : 8400009, Los Angeles
Menerima pesertaFase 4
Usia 12 ke atas · Semua jenis kelamin · Diperbarui 18 Nov 2025 · NCT06941870

Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.