Beranda › Kesalahan Bawaan Metabolisme › California
Uji klinis Kesalahan Bawaan Metabolisme di California
5 studi untuk Kesalahan Bawaan Metabolisme mencari peserta di lokasi di California.
Kota di California
Teks studi resmi (Bahasa Inggris)
A Long-Term Observational Study of Patients With Fucosidosis
- Children's Hospital of Orange County, Orange
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 17 Sep 2026 · NCT07615400Registry of Patients Diagnosed With Lysosomal Storage Diseases
- University of California San Francisco, San Francisco
Menerima pesertaStudi observasional
Hingga usia 64 · Semua jenis kelamin · Diperbarui 8 Apr 2026 · NCT05619900A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
- Ronald Reagan UCLA Medical Center, Los Angeles
- University of Stanford Medical Center, Palo Alto
Menerima pesertaFase 1/2
Usia 1 ke atas · Semua jenis kelamin · Diperbarui 23 Mar 2026 · NCT05130437Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- UCSD Altman Clinical and Transalational Research Institute Building, Los Angeles
- Ronald Reagan UCLA Medical Center, Los Angeles
- Lucile Packard Children's Hospital Stanford, Stanford
Menerima pesertaFase 1/2
Semua usia · Semua jenis kelamin · Diperbarui 22 Jan 2026 · NCT04159103An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705
- UCLA Medical Center, Los Angeles
- Lucile Packard Children's Hospital at Stanford, Palo Alto
- Altman Clinical and Translational Research Institution, San Diego
Menerima pesertaFase 1/2
Usia 1 ke atas · Semua jenis kelamin · Diperbarui 23 Des 2025 · NCT05295433Dari ClinicalTrials.gov, data diambil 3 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.