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Uji klinis Kesalahan Bawaan Metabolisme di Pennsylvania

6 studi untuk Kesalahan Bawaan Metabolisme mencari peserta di lokasi di Pennsylvania.

Kota di Pennsylvania

Teks studi resmi (Bahasa Inggris)

Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia

  • Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaStudi observasionalSukarelawan sehat diterima
1 Month – 100 Years · Semua jenis kelamin · Diperbarui 28 Sep 2026 · NCT02890342

Clinical and Laboratory Study of Methylmalonic Acidemia

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaStudi observasionalSukarelawan sehat diterima
1 Month – 115 Years · Semua jenis kelamin · Diperbarui 10 Sep 2026 · NCT00078078

Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT

  • Children's Hospital of Philadelphia, Philadelphia
Menerima pesertaFase 1/2
1 Month – 25 Years · Semua jenis kelamin · Diperbarui 15 Apr 2026 · NCT06839456

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • The Children's Hospital of Philadelphia (CHOP), Philadelphia
Menerima pesertaFase 1/2
Usia 1 ke atas · Semua jenis kelamin · Diperbarui 23 Mar 2026 · NCT05130437

Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC

  • Children's Hospital of Philadelphia, Philadelphia
Menerima pesertaFase awal 1
Hingga usia 30 · Semua jenis kelamin · Diperbarui 20 Feb 2026 · NCT02356653

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Children's Hospital of Philadelphia (CHOP), Philadelphia
Menerima pesertaFase 1/2
Semua usia · Semua jenis kelamin · Diperbarui 22 Jan 2026 · NCT04159103

Dari ClinicalTrials.gov, data diambil 4 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.