Beranda › Kesalahan Bawaan Metabolisme › Pennsylvania
Uji klinis Kesalahan Bawaan Metabolisme di Pennsylvania
6 studi untuk Kesalahan Bawaan Metabolisme mencari peserta di lokasi di Pennsylvania.
Kota di Pennsylvania
Teks studi resmi (Bahasa Inggris)
Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia
- Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaStudi observasionalSukarelawan sehat diterima
1 Month – 100 Years · Semua jenis kelamin · Diperbarui 28 Sep 2026 · NCT02890342Clinical and Laboratory Study of Methylmalonic Acidemia
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaStudi observasionalSukarelawan sehat diterima
1 Month – 115 Years · Semua jenis kelamin · Diperbarui 10 Sep 2026 · NCT00078078Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT
- Children's Hospital of Philadelphia, Philadelphia
Menerima pesertaFase 1/2
1 Month – 25 Years · Semua jenis kelamin · Diperbarui 15 Apr 2026 · NCT06839456A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
- The Children's Hospital of Philadelphia (CHOP), Philadelphia
Menerima pesertaFase 1/2
Usia 1 ke atas · Semua jenis kelamin · Diperbarui 23 Mar 2026 · NCT05130437Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC
- Children's Hospital of Philadelphia, Philadelphia
Menerima pesertaFase awal 1
Hingga usia 30 · Semua jenis kelamin · Diperbarui 20 Feb 2026 · NCT02356653Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- Children's Hospital of Philadelphia (CHOP), Philadelphia
Menerima pesertaFase 1/2
Semua usia · Semua jenis kelamin · Diperbarui 22 Jan 2026 · NCT04159103Dari ClinicalTrials.gov, data diambil 4 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.