Beranda › Mukopolisakaridosis IV › California
Uji klinis Mukopolisakaridosis IV di California
6 studi untuk Mukopolisakaridosis IV mencari peserta di lokasi di California.
Teks studi resmi (Bahasa Inggris)
Prospective Clinical Assessment Study in Children With Hypochondroplasia
- UCSF Benioff Children's Hospital, Oakland
Menerima pesertaStudi observasional
30 Months – 16 Years · Semua jenis kelamin · Diperbarui 16 Jul 2026 · NCT06410976Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH)
- UCSF Benioff Children's Hospital, Oakland
Menerima pesertaFase 2
0 Years – 32 Months · Semua jenis kelamin · Diperbarui 13 Jul 2026 · NCT07169279A Study Evaluating the Impact of Regular FODMAP-targeting Digestive Enzyme Blend Use on Gastrointestinal Symptoms in Individuals With Self-Reported Bloating
- People Science, Los Angeles
Menerima pesertaSukarelawan sehat diterima
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 15 Mei 2026 · NCT07591584Registry of Patients Diagnosed With Lysosomal Storage Diseases
- University of California San Francisco, San Francisco
Menerima pesertaStudi observasional
Hingga usia 64 · Semua jenis kelamin · Diperbarui 8 Apr 2026 · NCT05619900PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
- University of California, San Francisco
Menerima pesertaFase 1
Usia 18 hingga 50 · Wanita · Diperbarui 17 Mar 2026 · NCT04532047Cardiac Structure and Function in MPS
- Children'S Hospital of Orange County, Orange
Menerima pesertaStudi observasionalSukarelawan sehat diterima
Usia 0 hingga 99 · Semua jenis kelamin · Diperbarui 26 Jan 2026 · NCT07361536Dari ClinicalTrials.gov, data diambil 6 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.