Beranda › Distrofi Miotonik › New York
Uji klinis Distrofi Miotonik di New York
8 studi untuk Distrofi Miotonik mencari peserta di lokasi di New York.
Kota di New York
Teks studi resmi (Bahasa Inggris)
Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
- University of Rochester Medical Center, Rochester
Menerima pesertaFase 3
Usia 16 ke atas · Semua jenis kelamin · Diperbarui 1 Okt 2026 · NCT07486934A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
- Columbia University Medical Center - Neurological Institute, 710 W. 168th, 2nd floor, suite 204 - Site Number : 8400003, New York
Menerima pesertaFase 1/2
Usia 10 hingga 55 · Semua jenis kelamin · Diperbarui 21 Sep 2026 · NCT06844214DMCRN-02-001: Assessing Pediatric Endpoints in DM1
- University of Rochester Medical Center, Rochester
Menerima pesertaStudi observasional
59 Months · Semua jenis kelamin · Diperbarui 10 Jun 2026 · NCT05224778Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
- University of Rochester, Rochester
Menerima pesertaStudi observasional
Usia 18 hingga 70 · Semua jenis kelamin · Diperbarui 10 Jun 2026 · NCT03981575Remote Assessments and Genetic Determinants of Congenital and Childhood Myotonic Dystrophy
- University of Rochester, Rochester
Menerima pesertaStudi observasional
Usia 0 hingga 17 · Semua jenis kelamin · Diperbarui 5 Jun 2026 · NCT07630389Remote Assessments and Genetic Determinants of Myotonic Dystrophy
- University of Rochester, Rochester
Menerima pesertaStudi observasional
Usia 18 hingga 88 · Semua jenis kelamin · Diperbarui 1 Apr 2026 · NCT07505342Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
- University of Rochester Medical Center, Department of Neurology, Rochester
Menerima pesertaStudi observasionalSukarelawan sehat diterima
Semua usia · Semua jenis kelamin · Diperbarui 15 Okt 2025 · NCT00082108Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy
- University of Rochester - Medical Center, Rochester
Menerima pesertaFase 2/3
Usia 6 hingga 45 · Semua jenis kelamin · Diperbarui 28 Mei 2025 · NCT05004129Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.