🔎 Trials Near Me

Beranda › Distrofi Miotonik › Virginia

Uji klinis Distrofi Miotonik di Virginia

8 studi untuk Distrofi Miotonik mencari peserta di lokasi di Virginia.

Kota di Virginia

Teks studi resmi (Bahasa Inggris)

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

  • Virginia Commonwealth University - Biotech One, Richmond
Menerima pesertaFase 3
Usia 16 ke atas · Semua jenis kelamin · Diperbarui 1 Okt 2026 · NCT07486934

A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1

  • Virginia Commonwealth University Medical Center- Site Number : 8400006, Richmond
Menerima pesertaFase 1/2
Usia 10 hingga 55 · Semua jenis kelamin · Diperbarui 21 Sep 2026 · NCT06844214

Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension

  • Virginia Commonwealth University, Richmond
Menerima pesertaStudi observasional
Usia 18 hingga 70 · Semua jenis kelamin · Diperbarui 4 Sep 2026 · NCT07700225

Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

  • Virginia Commonwealth University, Richmond
Menerima pesertaStudi observasional
Usia 3 hingga 17 · Semua jenis kelamin · Diperbarui 11 Agu 2026 · NCT06747884

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

  • Virginia Commonwealth University, Richmond
Menerima pesertaStudi observasional
59 Months · Semua jenis kelamin · Diperbarui 10 Jun 2026 · NCT05224778

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

  • Virginia Commonwealth University, Richmond
Menerima pesertaStudi observasional
Usia 18 hingga 70 · Semua jenis kelamin · Diperbarui 10 Jun 2026 · NCT03981575

Study of ATX-01 in Participants With DM1

  • Virginia Commonwealth University, Richmond
Menerima pesertaFase 1/2
Usia 18 hingga 64 · Semua jenis kelamin · Diperbarui 10 Feb 2026 · NCT06300307

Long-Term Development of Muscular Dystrophy Outcome Assessments

  • Virginia Commonwealth University, Richmond
Menerima pesertaStudi observasional
Usia 6 hingga 50 · Semua jenis kelamin · Diperbarui 18 Nov 2025 · NCT05989620

Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.