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Uji klinis Penyakit Pelizaeus-Merzbacher di Pennsylvania

4 studi untuk Penyakit Pelizaeus-Merzbacher mencari peserta di lokasi di Pennsylvania.

Kota di Pennsylvania

Teks studi resmi (Bahasa Inggris)

Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease

  • Ionis Investigative Site, Philadelphia
Menerima pesertaStudi observasional
6 Months – 17 Years · Pria · Diperbarui 2 Okt 2026 · NCT05659901

Longitudinal Study of Neurodegenerative Disorders

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 9 Feb 2026 · NCT03333200

Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)

  • Ionis Investigative Site, Philadelphia
Menerima pesertaFase 1
Usia 2 hingga 17 · Pria · Diperbarui 12 Des 2025 · NCT06150716

The Myelin Disorders Biorepository Project

  • The Children's Hospital of Philadelphia, Philadelphia
  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh Medical Center, Pittsburgh
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 23 Okt 2025 · NCT03047369

Dari ClinicalTrials.gov, data diambil 6 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.