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Uji klinis Fenilketonuria di Pennsylvania

8 studi untuk Fenilketonuria mencari peserta di lokasi di Pennsylvania.

Kota di Pennsylvania

Teks studi resmi (Bahasa Inggris)

A Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-181 in Subjects With Phenylketonuria

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaFase 1
Usia 18 hingga 69 · Semua jenis kelamin · Diperbarui 28 Sep 2026 · NCT07241234

A Study of MZE782 in Adults With PKU

  • Clinic for Special Children, Gordonville
Menerima pesertaFase 2
Usia 18 hingga 75 · Semua jenis kelamin · Diperbarui 20 Agu 2026 · NCT07694440

AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)

  • University of Pittsburgh Medical Center, Pittsburgh
Menerima pesertaFase 1/2
Usia 18 hingga 55 · Semua jenis kelamin · Diperbarui 18 Agu 2026 · NCT06332807

A Study of JNT-517 in Participants With Phenylketonuria (PKU)

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaFase 3
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 8 Jul 2026 · NCT06971731

Immune Modulation During Palynziq® Treatment in Adults (IMPALA)

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Philadelphia
Menerima pesertaFase 4
Usia 18 hingga 65 · Semua jenis kelamin · Diperbarui 17 Jun 2026 · NCT07477691

A Long-Term Study of JNT-517 in Participants With Phenylketonuria

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaFase 3
Usia 4 ke atas · Semua jenis kelamin · Diperbarui 1 Mei 2026 · NCT06628128

A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)

  • University of Pittsburgh Medical Center, Pittsburgh
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 25 Mar 2026 · NCT05813678

A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)

  • University of Pittsburgh Medical Center, Pittsburgh
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 24 Mar 2026 · NCT06305234

Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.