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Uji klinis Asidemia Propionik di Pennsylvania

4 studi untuk Asidemia Propionik mencari peserta di lokasi di Pennsylvania.

Kota di Pennsylvania

Teks studi resmi (Bahasa Inggris)

Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia

  • Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaStudi observasionalSukarelawan sehat diterima
1 Month – 100 Years · Semua jenis kelamin · Diperbarui 28 Sep 2026 · NCT02890342

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • The Children's Hospital of Philadelphia (CHOP), Philadelphia
Menerima pesertaFase 1/2
Usia 1 ke atas · Semua jenis kelamin · Diperbarui 23 Mar 2026 · NCT05130437

A Retrospective Study to Characterize Participants With Propionic Acidemia

  • Children's Hospital of Philadelphia, Philadelphia
Menerima pesertaStudi observasional
Usia 2 ke atas · Semua jenis kelamin · Diperbarui 5 Feb 2026 · NCT05769621

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Children's Hospital of Philadelphia (CHOP), Philadelphia
Menerima pesertaFase 1/2
Semua usia · Semua jenis kelamin · Diperbarui 22 Jan 2026 · NCT04159103

Dari ClinicalTrials.gov, data diambil 3 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.