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Beranda › Penyakit Langka › Massachusetts

Uji klinis Penyakit Langka di Massachusetts

11 studi untuk Penyakit Langka mencari peserta di lokasi di Massachusetts.

Kota di Massachusetts

Teks studi resmi (Bahasa Inggris)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • Massachusetts General Hospital, Boston
  • Boston Children s Hospital, Boston
  • Brigham and Women's Hospital, Boston
  • dan 1 lainnya
Menerima pesertaStudi observasionalSukarelawan sehat diterima
1 Month – 100 Years · Semua jenis kelamin · Diperbarui 2 Okt 2026 · NCT02450851

RAPA-501 Therapy for ALS

  • Massachusetts General Hospital, Boston
Menerima pesertaFase 2/3
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 29 Sep 2026 · NCT04220190

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

  • Boston Children's Hospital, Boston
  • University of Massachusetts Chan Medical School, Worcester
Menerima pesertaStudi observasional
Usia 6 ke atas · Semua jenis kelamin · Diperbarui 2 Jul 2026 · NCT07127978

Direct to Patient Minimal Risk Biospecimen and Data Collection Research

  • Joined Bio, Lexington
Menerima pesertaStudi observasionalSukarelawan sehat diterima
Usia 18 hingga 90 · Semua jenis kelamin · Diperbarui 5 Mei 2026 · NCT07128966

A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease

  • Beth Israel Deaconess Medical Center, Boston
Menerima pesertaFase 1/2
Usia 25 hingga 65 · Semua jenis kelamin · Diperbarui 5 Mei 2026 · NCT06826612

A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

  • Massachusetts General Hospital (MGH); Center for Rare Neurological Diseases (CRND), Boston
Menerima pesertaFase 1/2
30 Months · Semua jenis kelamin · Diperbarui 17 Apr 2026 · NCT04998396

Gene Discovery Core, The Manton Center

  • Boston Children's Hospital, Boston
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 25 Mar 2026 · NCT02743845

Delineating the Molecular Spectrum and the Clinical, Imaging and Neuronal Phenotype of Chopra-Amiel-Gordon Syndrome

  • Boston Children's Hospital, Boston
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 17 Feb 2026 · NCT05528744

The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis

  • Massachusetts General Hospital, Boston
Menerima pesertaFase 2
Usia 12 ke atas · Semua jenis kelamin · Diperbarui 1 Jul 2025 · NCT04372615

A Multi-Site Leukopak Repository Providing Annotated Biospecimens for Approved Investigator-Directed Biomedical Research Initiatives

  • Sanguine Biosciences, Waltham
Menerima pesertaStudi observasionalSukarelawan sehat diterima
Usia 18 hingga 89 · Semua jenis kelamin · Diperbarui 6 Des 2024 · NCT05794217

Epilepsy Learning Healthcare System (ELHS)

  • Partners - Massachusetts General Hospital Epilepsy Service (MGH)/ Partners - Brigham and Women's (BWH), Boston
  • Brigham & Women's Hospital, Boston
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 30 Agu 2024 · NCT06265103

Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.