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Beranda › Penyakit Langka › North Carolina

Uji klinis Penyakit Langka di North Carolina

6 studi untuk Penyakit Langka mencari peserta di lokasi di North Carolina.

Kota di North Carolina

Teks studi resmi (Bahasa Inggris)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • Duke University Health System, Durham
Menerima pesertaStudi observasionalSukarelawan sehat diterima
1 Month – 100 Years · Semua jenis kelamin · Diperbarui 2 Okt 2026 · NCT02450851

Odevixibat Pregnancy and Lactation Surveillance Program: A Study to Evaluate the Safety of Odevixibat During Pregnancy and/or Lactation

  • Virtual Research Coordination Center Odevixibat (BYLVAY) Pregnancy Surveillance Program, Wilmington
Menerima pesertaStudi observasional
Semua usia · Wanita · Diperbarui 1 Okt 2026 · NCT06258902

Elafibranor Pregnancy Surveillance Program: A Study to Evaluate the Safety of Elafibranor During Pregnancy

  • Virtual Research Coordination Center, Wilmington
Menerima pesertaStudi observasional
Semua usia · Wanita · Diperbarui 31 Agu 2026 · NCT07556913

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

  • Duke University / Lenox Baker Children's Hospital, Durham
Menerima pesertaStudi observasional
Usia 6 ke atas · Semua jenis kelamin · Diperbarui 2 Jul 2026 · NCT07127978

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Duke University Medical Center, Durham
Menerima pesertaFase 2
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 23 Jun 2026 · NCT07123155

The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis

  • Wake Forest University Health Sciences, Winston-Salem
Menerima pesertaFase 2
Usia 12 ke atas · Semua jenis kelamin · Diperbarui 1 Jul 2025 · NCT04372615

Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.