Beranda › Sindrom Rett › Pennsylvania
Uji klinis Sindrom Rett di Pennsylvania
5 studi untuk Sindrom Rett mencari peserta di lokasi di Pennsylvania.
Kota di Pennsylvania
Teks studi resmi (Bahasa Inggris)
A Phase 3 Study of Fenfluramine Hydrochloride in Rett Syndrome
- Ep0247 21003, Philadelphia
Menerima pesertaFase 3
Usia 5 hingga 35 · Semua jenis kelamin · Diperbarui 2 Okt 2026 · NCT07503444Rett Syndrome Registry
- Children's Hospital of Philadelphia, Philadelphia
Menerima pesertaStudi observasional
Usia 0 hingga 99 · Semua jenis kelamin · Diperbarui 30 Jun 2026 · NCT05432349To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome
- Biomed Testing Facility #BIO-17-19104, Philadelphia
Menerima pesertaFase 3
Usia 5 hingga 20 · Wanita · Diperbarui 27 Mar 2026 · NCT06840496ATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION440 in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome (MDS)
- Children's Hospital of Philadelphia, Philadelphia
Menerima pesertaFase 1/2
Usia 2 hingga 65 · Pria · Diperbarui 24 Mar 2026 · NCT06430385Neurophysiologic Biomarkers in Rett Syndrome
- Children's Hospital of Philadelphia, Philadelphia
Menerima pesertaStudi observasionalSukarelawan sehat diterima
Usia 1 hingga 18 · Wanita · Diperbarui 20 Okt 2025 · NCT05932589Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.