Beranda › Atrofi Otot Tulang Belakang › Arkansas
Uji klinis Atrofi Otot Tulang Belakang di Arkansas
4 studi untuk Atrofi Otot Tulang Belakang mencari peserta di lokasi di Arkansas.
Kota di Arkansas
Teks studi resmi (Bahasa Inggris)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- University of Arkansas for Medical Sciences, Little Rock
Menerima pesertaFase 4
3 Months – 24 Months · Semua jenis kelamin · Diperbarui 2 Okt 2026 · NCT05861986A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Arkansas Children's Hospital, Little Rock
Menerima pesertaFase 2
Usia 5 hingga 17 · Semua jenis kelamin · Diperbarui 14 Sep 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- University of Arkansas for Medical Sciences, Little Rock
Menerima pesertaFase 4
3 Months – 24 Months · Semua jenis kelamin · Diperbarui 10 Sep 2026 · NCT05861999Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Arkansas Children's Hospital, Little Rock
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 31 Jan 2025 · NCT04174157Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.