Beranda › Atrofi Otot Tulang Belakang › Massachusetts
Uji klinis Atrofi Otot Tulang Belakang di Massachusetts
6 studi untuk Atrofi Otot Tulang Belakang mencari peserta di lokasi di Massachusetts.
Kota di Massachusetts
Teks studi resmi (Bahasa Inggris)
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
Menerima pesertaFase 2
Usia 5 hingga 17 · Semua jenis kelamin · Diperbarui 14 Sep 2026 · NCT07287982A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Boston Children's Hospital, Boston
Menerima pesertaFase 1
Usia 3 ke atas · Semua jenis kelamin · Diperbarui 3 Sep 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
Menerima peserta
Usia 3 ke atas · Semua jenis kelamin · Diperbarui 19 Agu 2026 · NCT05866419ALS/MND Natural History Study Data Repository
- Lahey Clinic, Burlington
Menerima pesertaStudi observasional
Usia 18 hingga 90 · Semua jenis kelamin · Diperbarui 20 Mei 2026 · NCT05966038Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Boston Children's Hospital, Boston
Menerima pesertaStudi observasionalSukarelawan sehat diterima
Usia 5 ke atas · Semua jenis kelamin · Diperbarui 9 Apr 2026 · NCT06839469A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Boston Children's Hospital, Boston
Menerima pesertaStudi observasional
Usia 18 hingga 54 · Wanita · Diperbarui 9 Mar 2026 · NCT05789758Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.