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Uji klinis Atrofi Otot Tulang Belakang di Virginia

7 studi untuk Atrofi Otot Tulang Belakang mencari peserta di lokasi di Virginia.

Kota di Virginia

Teks studi resmi (Bahasa Inggris)

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam

  • Childrens Hospital of the Kings Daughter Norfolk, Norfolk
Menerima pesertaFase 3
Usia 15 hingga 60 · Semua jenis kelamin · Diperbarui 2 Okt 2026 · NCT07444476

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Childrens Hospital of The Kings Daughters, Norfolk
Menerima pesertaFase 2
Usia 5 hingga 17 · Semua jenis kelamin · Diperbarui 14 Sep 2026 · NCT07287982

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Stacey Hall Developmental Pediatrics, Charlottesville
  • Children's Hospital of the King's Daughters_Norfolk, Norfolk
Menerima pesertaFase 1
Usia 3 ke atas · Semua jenis kelamin · Diperbarui 3 Sep 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • University of Virginia, Charlottesville
  • Childrens Hospital of the King's Daughters, Norfolk
Menerima peserta
Usia 3 ke atas · Semua jenis kelamin · Diperbarui 19 Agu 2026 · NCT05866419

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

  • Childrens Hospital of the Kings Daughter Norfolk, Norfolk
Menerima pesertaFase 3
0 Days – 42 Days · Semua jenis kelamin · Diperbarui 18 Agu 2026 · NCT07221669

ALS/MND Natural History Study Data Repository

  • Virginia Commonwealth University, Richmond
Menerima pesertaStudi observasional
Usia 18 hingga 90 · Semua jenis kelamin · Diperbarui 20 Mei 2026 · NCT05966038

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • University of Virginia Health System, Charlottesville
  • Children's Hospital of The King's Daughters, Norfolk
  • Virginia Commonwealth University Health System, Richmond
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 31 Jan 2025 · NCT04174157

Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.