ペンシルベニアにおける脊髄性筋萎縮症の臨床試験
ペンシルベニア内の拠点で、脊髄性筋萎縮症に関する8件の研究が参加者を募集しています。
ペンシルベニア内の都市
公式研究テキスト（英語）
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- Children'S Hospital of Philadelphia, Philadelphia
被験者募集中第4相
3 Months – 24 Months · 全性別 · 2026/10/02更新 · NCT05861986A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
- The Children's Hospital of Philadelphia, Philadelphia
被験者募集中第2相
2歳以下 · 全性別 · 2026/10/02更新 · NCT07047144A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Children's Hospital Philadelphia - Neurology, Philadelphia
被験者募集中第2相
5歳〜17歳 · 全性別 · 2026/09/14更新 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- Children'S Hospital of Philadelphia, Philadelphia
被験者募集中第4相
3 Months – 24 Months · 全性別 · 2026/09/10更新 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Milton S. Hershey Medical Center | Pennsylvania State University_Hershey, Hershey
- Children's Hospital of Philadelphia, Philadelphia
被験者募集中第1相
3歳以上 · 全性別 · 2026/09/03更新 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Penn State Milton S. Hershey Medical Center, Hershey
- Children's Hospital Philadelphia, Philadelphia
被験者募集中
3歳以上 · 全性別 · 2026/08/19更新 · NCT05866419ALS/MND Natural History Study Data Repository
- Thomas Jefferson University, Philadelphia
- Temple University Lewis Katz School of Medicine, Philadelphia
- University of Pittsburgh, Pittsburgh
被験者募集中観察研究
18歳〜90歳 · 全性別 · 2026/05/20更新 · NCT05966038Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Penn State Hershey, Hershey
- University of Pittsburgh Medical Center, Pittsburgh
被験者募集中観察研究
全年齢 · 全性別 · 2025/01/31更新 · NCT04174157ClinicalTrials.govより、2026/10/05時点のデータを取得。各研究には独自の参加資格があり、参加可否は研究チームが決定します。