Pradžia › Adrenoleukodistrofija › Pennsylvania
Adrenoleukodistrofija klinikiniai tyrimai Pennsylvania
4 tyrimai dėl Adrenoleukodistrofija ieško dalyvių vietose Pennsylvania.
Miestai Pennsylvania
Oficialus tyrimo tekstas (anglų kalba)
Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Renkami dalyviaiStebimasis tyrimas
2 Months – 60 Years · Visoms lytims · Atnaujinta 2026-01-13 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Renkami dalyviai2 fazė
2 Months – 55 Years · Visoms lytims · Atnaujinta 2025-12-15 · NCT01962415The Myelin Disorders Biorepository Project
- The Children's Hospital of Philadelphia, Philadelphia
- University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center, Pittsburgh
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2025-10-23 · NCT03047369A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel
- Children's Hospital of Philadelphia, Philadelphia
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Vyrams · Atnaujinta 2025-07-02 · NCT06224413Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.