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beta-Thalassemia clinical trials in Pennsylvania
5 studies for beta-Thalassemia are looking for participants at sites in Pennsylvania.
Cities in Pennsylvania
ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia
- Children's Hospital of Philadelphia, Philadelphia
RecruitingPhase 1/2
Ages 18 to 40 · All sexes · Updated Sep 23, 2026 · NCT06364774T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias
- Children's Hospital of Pittsburgh of UPMC, Pittsburgh
RecruitingPhase 1/2
Ages 5 to 40 · All sexes · Updated Aug 13, 2026 · NCT03653338Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RecruitingObservational study
2 Months – 60 Years · All sexes · Updated Jan 13, 2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RecruitingPhase 2
2 Months – 55 Years · All sexes · Updated Dec 15, 2025 · NCT01962415A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel
- Children's Hospital of Philadelphia, Philadelphia
RecruitingObservational study
All ages · All sexes · Updated Feb 11, 2025 · NCT06271512From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.