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Oficialus tyrimo tekstas (anglų kalba)

TRITON-CM: A Study to Evaluate Nucresiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy

  • Clinical Trial Site, Boston
  • Clinical Trial Site, Boston
Renkami dalyviai3 fazė
Amžius nuo 18 iki 85 · Visoms lytims · Atnaujinta 2026-09-16 · NCT07052903

DemonsTTRate: A Global, Observational, Multicenter, Long-term Study of Patients With ATTR-CM in a Real-World Setting

  • Clinical Trial Site, Boston
Renkami dalyviaiStebimasis tyrimas
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-09-09 · NCT07358078

Clinical Course Of Disease In Participants With FA-CM

  • Boston Children's Hospital, Boston
Renkami dalyviaiStebimasis tyrimas
Amžius 6 ir vyresni · Visoms lytims · Atnaujinta 2026-09-02 · NCT06865482

Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant

  • Massachusetts General Hospital, Boston
  • Brigham and Women's Hospital, Boston
  • Boston University (BU) School of Medicine, Boston
Renkami dalyviai3 fazė
Amžius nuo 18 iki 75 · Visoms lytims · Atnaujinta 2026-08-04 · NCT06563895

The PIVATAL Study -Study of Ventricular Arrhythmia (VTA) Ablation in Left Ventricular Assist Device (LVAD) Patients

  • Tufts Medical Center, Boston
Renkami dalyviai4 fazė
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-07-14 · NCT05034432

A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease

  • Boston Children's Hospital, Boston
Renkami dalyviai2 fazė
Amžius 8 ir vyresni · Vyrams · Atnaujinta 2026-05-04 · NCT06092034

MAGNITUDE: A Phase 3 Study of NTLA-2001 in Participants With Transthyretin Amyloidosis With Cardiomyopathy (ATTR-CM)

  • Brigham and Women's Hospital, Boston
  • Boston University School of Medicine, Boston
Renkami dalyviai3 fazė
Amžius nuo 18 iki 90 · Visoms lytims · Atnaujinta 2026-03-27 · NCT06128629

PKP2-ACM Natural History Study

  • Boston Children's Hospital, Boston
Renkami dalyviaiStebimasis tyrimas
Amžius 12 ir vyresni · Visoms lytims · Atnaujinta 2026-02-27 · NCT06644742

Molecular Imaging of Primary Amyloid Cardiomyopathy

  • Brigham and Womens' Hospital, Boston
Renkami dalyviai
Amžius nuo 18 iki 99 · Visoms lytims · Atnaujinta 2025-11-14 · NCT02641145

Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.