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Kardiomiopatija klinikiniai tyrimai Pennsylvania
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Oficialus tyrimo tekstas (anglų kalba)
TRITON-CM: A Study to Evaluate Nucresiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy
- Clinical Trial Site, Lancaster
- Clinical Trial Site, Philadelphia
Renkami dalyviai3 fazė
Amžius nuo 18 iki 85 · Visoms lytims · Atnaujinta 2026-09-16 · NCT07052903DemonsTTRate: A Global, Observational, Multicenter, Long-term Study of Patients With ATTR-CM in a Real-World Setting
- Clinical Trial Site, Philadelphia
Renkami dalyviaiStebimasis tyrimas
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-09-09 · NCT07358078Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant
- Penn Presbyterian Medical Center, Philadelphia
- University of Pittsburgh Medical Center, Presbyterian Hospital, Pittsburgh
Renkami dalyviai3 fazė
Amžius nuo 18 iki 75 · Visoms lytims · Atnaujinta 2026-08-04 · NCT06563895The PIVATAL Study -Study of Ventricular Arrhythmia (VTA) Ablation in Left Ventricular Assist Device (LVAD) Patients
- University of Pennsylvania, Philadelphia
- UPMC, Pittsburgh
Renkami dalyviai4 fazė
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-07-14 · NCT05034432A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease
- Children's Hospital of Philadelphia, Philadelphia
Renkami dalyviai2 fazė
Amžius 8 ir vyresni · Vyrams · Atnaujinta 2026-05-04 · NCT06092034MAGNITUDE: A Phase 3 Study of NTLA-2001 in Participants With Transthyretin Amyloidosis With Cardiomyopathy (ATTR-CM)
- Penn Presbyterian Medical Center, Philadelphia
- Allegheny General Hospital, Pittsburgh
- University of Pittsburgh Medical Center, Pittsburgh
Renkami dalyviai3 fazė
Amžius nuo 18 iki 90 · Visoms lytims · Atnaujinta 2026-03-27 · NCT06128629Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.