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Fabry liga klinikiniai tyrimai Minesota

4 tyrimai dėl Fabry liga ieško dalyvių vietose Minesota.

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Oficialus tyrimo tekstas (anglų kalba)

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • MHealth Fairview University of Minnesota Medical Center East Bank, Minneapolis
Renkami dalyviai1/2 fazė
Amžius nuo 18 iki 65 · Vyrams · Atnaujinta 2026-09-24 · NCT06270316

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • University of Minnesota Masonic Children's Hospital, Minneapolis
Renkami dalyviai3 fazė
Amžius nuo 2 iki 11 · Visoms lytims · Atnaujinta 2026-09-01 · NCT06904261

Natural History and Structural Functional Relationships in Fabry Renal Disease Treatment Outcomes(Changes)in Fabry Renal Disease Study

  • University of Minnesota, Minneapolis
  • Universtity of Minnesota, Department of Pediatric Nephrology, Minneapolis
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 1 iki 75 · Visoms lytims · Atnaujinta 2026-08-14 · NCT01581424

Fabry Disease Registry & Pregnancy Sub-registry

  • Children's Hospitals and Clinics of Minnesota- Site Number : 840114, Minneapolis
  • M Health Fairview University of Minnesota Medical Center - West Bank- Site Number : 840076, Minneapolis
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2026-06-23 · NCT00196742

Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.