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Fabry liga klinikiniai tyrimai Pennsylvania
5 tyrimai dėl Fabry liga ieško dalyvių vietose Pennsylvania.
Miestai Pennsylvania
Oficialus tyrimo tekstas (anglų kalba)
Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Renkami dalyviai1/2 fazė
Amžius nuo 18 iki 65 · Vyrams · Atnaujinta 2026-09-24 · NCT06270316A Study of Patients With Fabry Disease (US Specific)
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Renkami dalyviaiStebimasis tyrimas
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-09-09 · NCT06906367A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Renkami dalyviai3 fazė
Amžius nuo 2 iki 11 · Visoms lytims · Atnaujinta 2026-09-01 · NCT06904261Fabry Disease Registry & Pregnancy Sub-registry
- Geisinger Medical Center- Site Number : 840111, Danville
- Penn State University Medical Center-Neurology- Site Number : 840104, Hershey
- Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
- ir dar 2
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2026-06-23 · NCT00196742A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding
- Amicus Therapeutics, Inc. Pregnancy Registry, Philadelphia
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Moterims · Atnaujinta 2025-07-08 · NCT04252066Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.