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Fabry liga klinikiniai tyrimai Pennsylvania

5 tyrimai dėl Fabry liga ieško dalyvių vietose Pennsylvania.

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Oficialus tyrimo tekstas (anglų kalba)

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Renkami dalyviai1/2 fazė
Amžius nuo 18 iki 65 · Vyrams · Atnaujinta 2026-09-24 · NCT06270316

A Study of Patients With Fabry Disease (US Specific)

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Renkami dalyviaiStebimasis tyrimas
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-09-09 · NCT06906367

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Renkami dalyviai3 fazė
Amžius nuo 2 iki 11 · Visoms lytims · Atnaujinta 2026-09-01 · NCT06904261

Fabry Disease Registry & Pregnancy Sub-registry

  • Geisinger Medical Center- Site Number : 840111, Danville
  • Penn State University Medical Center-Neurology- Site Number : 840104, Hershey
  • Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
  • ir dar 2
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2026-06-23 · NCT00196742

A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding

  • Amicus Therapeutics, Inc. Pregnancy Registry, Philadelphia
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Moterims · Atnaujinta 2025-07-08 · NCT04252066

Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.