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Fabry liga klinikiniai tyrimai Virginia

6 tyrimai dėl Fabry liga ieško dalyvių vietose Virginia.

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Oficialus tyrimo tekstas (anglų kalba)

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • Lysosomal & Rare Disorders Research and Treatment Center, Inc, Fairfax
Renkami dalyviai1/2 fazė
Amžius nuo 18 iki 65 · Vyrams · Atnaujinta 2026-09-24 · NCT06270316

A Study of Patients With Fabry Disease (US Specific)

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
Renkami dalyviaiStebimasis tyrimas
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-09-09 · NCT06906367

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
Renkami dalyviai3 fazė
Amžius nuo 2 iki 11 · Visoms lytims · Atnaujinta 2026-09-01 · NCT06904261

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease

  • Lysosomal and Rare Disorders Research and Treatment Center Inc, Fairfax
Renkami dalyviai2/3 fazė
Amžius nuo 2 iki 17 · Visoms lytims · Atnaujinta 2026-08-10 · NCT06328608

Fabry Disease Registry & Pregnancy Sub-registry

  • O & O Alpan- Site Number : 840025, Fairfax
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2026-06-23 · NCT00196742

A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients

  • Lysosomal & Rare Disorder Research & Treatment Center (LRDRTC), Fairfax
Renkami dalyviaiStebimasis tyrimas
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2025-11-14 · NCT06663358

Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.