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Glikogeno kaupimosi liga, II tipas klinikiniai tyrimai Kalifornija
5 tyrimai dėl Glikogeno kaupimosi liga, II tipas ieško dalyvių vietose Kalifornija.
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Oficialus tyrimo tekstas (anglų kalba)
A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease
- University of California-Irvine, Irvine
Renkami dalyviai1 fazė
Amžius nuo 18 iki 75 · Visoms lytims · Atnaujinta 2026-08-17 · NCT07354724A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
- University of California, Irvine (UCI), Irvine
- Stanford Neuroscience Health Center, Palo Alto
Renkami dalyviai1/2 fazė
Amžius nuo 18 iki 65 · Visoms lytims · Atnaujinta 2026-07-20 · NCT07282847Pompe Disease Registry Protocol
- University of California at Irvine- Site Number : 840036, Irvine
- Southern California Permanente Medical Group- Site Number : 840108, Los Angeles
- Children's Hospital of Orange County- Site Number : 840074, Orange
- ir dar 3
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2026-06-23 · NCT00231400Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- University of California - Irvine Medical Center, Irvine
Renkami dalyviai2 fazė
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-06-23 · NCT07123155A Global Prospective Observational Registry of Patients With Pompe Disease
- University of California Irvine, Irvine
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2026-03-10 · NCT06121011Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.