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Glikogeno kaupimosi liga, II tipas klinikiniai tyrimai Misūris

6 tyrimai dėl Glikogeno kaupimosi liga, II tipas ieško dalyvių vietose Misūris.

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Oficialus tyrimo tekstas (anglų kalba)

A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease

  • Washington University School of Medicine, St Louis
Renkami dalyviai1 fazė
Amžius nuo 18 iki 75 · Visoms lytims · Atnaujinta 2026-08-17 · NCT07354724

Pompe Disease Registry Protocol

  • University of Missouri Health System Department of Genetics- Site Number : 840031, Columbia
  • Washington University- Site Number : 840100, St Louis
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2026-06-23 · NCT00231400

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Washington University in St. Louis, St Louis
Renkami dalyviai2 fazė
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-06-23 · NCT07123155

Pompe Pregnancy Sub-Registry

  • Washington University- Site Number : 150612, St Louis
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Moterims · Atnaujinta 2026-04-16 · NCT00567073

Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease

  • NextGen Precision Health Building, Clinical and Translational Science Unit, Columbia
Renkami dalyviai
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-03-17 · NCT07478172

A Global Prospective Observational Registry of Patients With Pompe Disease

  • Washington University School of Medicine, St Louis
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2026-03-10 · NCT06121011

Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.