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Glikogeno kaupimosi liga, II tipas klinikiniai tyrimai Pennsylvania
4 tyrimai dėl Glikogeno kaupimosi liga, II tipas ieško dalyvių vietose Pennsylvania.
Miestai Pennsylvania
Oficialus tyrimo tekstas (anglų kalba)
A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
- Hospital of the University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center (UPMC), Pittsburgh
Renkami dalyviai1/2 fazė
Amžius nuo 18 iki 65 · Visoms lytims · Atnaujinta 2026-07-20 · NCT07282847Pompe Disease Registry Protocol
- Penn State Health Milton South Hershey Medical Center- Site Number : 840126, Hershey
- Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
- Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
- ir dar 2
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2026-06-23 · NCT00231400Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- University of Pennsylvania, Philadelphia
- University of Pittsburgh School of Medicine, Pittsburgh
Renkami dalyviai2 fazė
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-06-23 · NCT07123155A Global Prospective Observational Registry of Patients With Pompe Disease
- University of Pennsylvania Perelman Center for Advanced Medicine, Philadelphia
- University of Pittsburgh, Pittsburgh
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2026-03-10 · NCT06121011Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.