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Metaboliniai sutrikimai klinikiniai tyrimai Pennsylvania

5 tyrimai dėl Metaboliniai sutrikimai ieško dalyvių vietose Pennsylvania.

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Oficialus tyrimo tekstas (anglų kalba)

Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia

  • Children's Hospital of Pittsburgh, Pittsburgh
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
1 Month – 100 Years · Visoms lytims · Atnaujinta 2026-09-28 · NCT02890342

Clinical and Laboratory Study of Methylmalonic Acidemia

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
1 Month – 115 Years · Visoms lytims · Atnaujinta 2026-09-10 · NCT00078078

A Study to Evaluate the Efficacy and Safety of Pegozafermin in Participants With Compensated Cirrhosis Due to MASH

  • 89bio Clinical Study Site, Philadelphia
  • 89bio Clinical Study Site, Pittsburgh
Renkami dalyviai3 fazė
Amžius nuo 18 iki 75 · Visoms lytims · Atnaujinta 2026-09-03 · NCT06419374

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • The Children's Hospital of Philadelphia (CHOP), Philadelphia
Renkami dalyviai1/2 fazė
Amžius 1 ir vyresni · Visoms lytims · Atnaujinta 2026-03-23 · NCT05130437

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Children's Hospital of Philadelphia (CHOP), Philadelphia
Renkami dalyviai1/2 fazė
Visi amžiai · Visoms lytims · Atnaujinta 2026-01-22 · NCT04159103

Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.