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Miotoninė distrofija klinikiniai tyrimai New York

8 tyrimai dėl Miotoninė distrofija ieško dalyvių vietose New York.

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Oficialus tyrimo tekstas (anglų kalba)

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

  • University of Rochester Medical Center, Rochester
Renkami dalyviai3 fazė
Amžius 16 ir vyresni · Visoms lytims · Atnaujinta 2026-10-01 · NCT07486934

A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1

  • Columbia University Medical Center - Neurological Institute, 710 W. 168th, 2nd floor, suite 204 - Site Number : 8400003, New York
Renkami dalyviai1/2 fazė
Amžius nuo 10 iki 55 · Visoms lytims · Atnaujinta 2026-09-21 · NCT06844214

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

  • University of Rochester Medical Center, Rochester
Renkami dalyviaiStebimasis tyrimas
59 Months · Visoms lytims · Atnaujinta 2026-06-10 · NCT05224778

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

  • University of Rochester, Rochester
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 18 iki 70 · Visoms lytims · Atnaujinta 2026-06-10 · NCT03981575

Remote Assessments and Genetic Determinants of Congenital and Childhood Myotonic Dystrophy

  • University of Rochester, Rochester
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 0 iki 17 · Visoms lytims · Atnaujinta 2026-06-05 · NCT07630389

Remote Assessments and Genetic Determinants of Myotonic Dystrophy

  • University of Rochester, Rochester
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 18 iki 88 · Visoms lytims · Atnaujinta 2026-04-01 · NCT07505342

Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry

  • University of Rochester Medical Center, Department of Neurology, Rochester
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Visi amžiai · Visoms lytims · Atnaujinta 2025-10-15 · NCT00082108

Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy

  • University of Rochester - Medical Center, Rochester
Renkami dalyviai2/3 fazė
Amžius nuo 6 iki 45 · Visoms lytims · Atnaujinta 2025-05-28 · NCT05004129

Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.