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Miotoninė distrofija klinikiniai tyrimai Virginia
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Oficialus tyrimo tekstas (anglų kalba)
Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
- Virginia Commonwealth University - Biotech One, Richmond
Renkami dalyviai3 fazė
Amžius 16 ir vyresni · Visoms lytims · Atnaujinta 2026-10-01 · NCT07486934A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
- Virginia Commonwealth University Medical Center- Site Number : 8400006, Richmond
Renkami dalyviai1/2 fazė
Amžius nuo 10 iki 55 · Visoms lytims · Atnaujinta 2026-09-21 · NCT06844214Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension
- Virginia Commonwealth University, Richmond
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 18 iki 70 · Visoms lytims · Atnaujinta 2026-09-04 · NCT07700225Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension
- Virginia Commonwealth University, Richmond
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 3 iki 17 · Visoms lytims · Atnaujinta 2026-08-11 · NCT06747884DMCRN-02-001: Assessing Pediatric Endpoints in DM1
- Virginia Commonwealth University, Richmond
Renkami dalyviaiStebimasis tyrimas
59 Months · Visoms lytims · Atnaujinta 2026-06-10 · NCT05224778Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
- Virginia Commonwealth University, Richmond
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 18 iki 70 · Visoms lytims · Atnaujinta 2026-06-10 · NCT03981575Study of ATX-01 in Participants With DM1
- Virginia Commonwealth University, Richmond
Renkami dalyviai1/2 fazė
Amžius nuo 18 iki 64 · Visoms lytims · Atnaujinta 2026-02-10 · NCT06300307Long-Term Development of Muscular Dystrophy Outcome Assessments
- Virginia Commonwealth University, Richmond
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 6 iki 50 · Visoms lytims · Atnaujinta 2025-11-18 · NCT05989620Iš ClinicalTrials.gov, duomenys gauti 2026-10-04. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.