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Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- Massachusetts General Hospital, Boston
- Boston Children s Hospital, Boston
- Brigham and Women's Hospital, Boston
- ir dar 1
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
1 Month – 100 Years · Visoms lytims · Atnaujinta 2026-10-02 · NCT02450851RAPA-501 Therapy for ALS
- Massachusetts General Hospital, Boston
Renkami dalyviai2/3 fazė
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-09-29 · NCT04220190A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy
- Boston Children's Hospital, Boston
- University of Massachusetts Chan Medical School, Worcester
Renkami dalyviaiStebimasis tyrimas
Amžius 6 ir vyresni · Visoms lytims · Atnaujinta 2026-07-02 · NCT07127978Direct to Patient Minimal Risk Biospecimen and Data Collection Research
- Joined Bio, Lexington
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Amžius nuo 18 iki 90 · Visoms lytims · Atnaujinta 2026-05-05 · NCT07128966A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease
- Beth Israel Deaconess Medical Center, Boston
Renkami dalyviai1/2 fazė
Amžius nuo 25 iki 65 · Visoms lytims · Atnaujinta 2026-05-05 · NCT06826612A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)
- Massachusetts General Hospital (MGH); Center for Rare Neurological Diseases (CRND), Boston
Renkami dalyviai1/2 fazė
30 Months · Visoms lytims · Atnaujinta 2026-04-17 · NCT04998396Gene Discovery Core, The Manton Center
- Boston Children's Hospital, Boston
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2026-03-25 · NCT02743845Delineating the Molecular Spectrum and the Clinical, Imaging and Neuronal Phenotype of Chopra-Amiel-Gordon Syndrome
- Boston Children's Hospital, Boston
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2026-02-17 · NCT05528744The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis
- Massachusetts General Hospital, Boston
Renkami dalyviai2 fazė
Amžius 12 ir vyresni · Visoms lytims · Atnaujinta 2025-07-01 · NCT04372615A Multi-Site Leukopak Repository Providing Annotated Biospecimens for Approved Investigator-Directed Biomedical Research Initiatives
- Sanguine Biosciences, Waltham
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Amžius nuo 18 iki 89 · Visoms lytims · Atnaujinta 2024-12-06 · NCT05794217Epilepsy Learning Healthcare System (ELHS)
- Partners - Massachusetts General Hospital Epilepsy Service (MGH)/ Partners - Brigham and Women's (BWH), Boston
- Brigham & Women's Hospital, Boston
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2024-08-30 · NCT06265103Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.