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Retto sindromas klinikiniai tyrimai Kalifornija
4 tyrimai dėl Retto sindromas ieško dalyvių vietose Kalifornija.
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Oficialus tyrimo tekstas (anglų kalba)
Rett Syndrome Registry
- Children's Hospital Los Angeles, Los Angeles
- UCSF Benioff Children's Hospital, Oakland
- Rady Children's Hospital - San Diego, San Diego
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 0 iki 99 · Visoms lytims · Atnaujinta 2026-06-30 · NCT05432349To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome
- Biomed Testing Facility # BIO-05-92093, La Jolla
- Biomed Testing Facility # BIO-04-90095, Los Angeles
- Biomed Testing Facility # BIO-03-95817, Sacramento
- ir dar 1
Renkami dalyviai3 fazė
Amžius nuo 5 iki 20 · Moterims · Atnaujinta 2026-03-27 · NCT06840496ATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION440 in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome (MDS)
- Rady Children's Hospital, San Diego
Renkami dalyviai1/2 fazė
Amžius nuo 2 iki 65 · Vyrams · Atnaujinta 2026-03-24 · NCT06430385Neurophysiologic Biomarkers in Rett Syndrome
- Children's Hospital of Los Angeles, Los Angeles
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Amžius nuo 1 iki 18 · Moterims · Atnaujinta 2025-10-20 · NCT05932589Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.