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Retto sindromas klinikiniai tyrimai Pennsylvania

5 tyrimai dėl Retto sindromas ieško dalyvių vietose Pennsylvania.

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Oficialus tyrimo tekstas (anglų kalba)

A Phase 3 Study of Fenfluramine Hydrochloride in Rett Syndrome

  • Ep0247 21003, Philadelphia
Renkami dalyviai3 fazė
Amžius nuo 5 iki 35 · Visoms lytims · Atnaujinta 2026-10-02 · NCT07503444

Rett Syndrome Registry

  • Children's Hospital of Philadelphia, Philadelphia
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 0 iki 99 · Visoms lytims · Atnaujinta 2026-06-30 · NCT05432349

To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome

  • Biomed Testing Facility #BIO-17-19104, Philadelphia
Renkami dalyviai3 fazė
Amžius nuo 5 iki 20 · Moterims · Atnaujinta 2026-03-27 · NCT06840496

ATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION440 in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome (MDS)

  • Children's Hospital of Philadelphia, Philadelphia
Renkami dalyviai1/2 fazė
Amžius nuo 2 iki 65 · Vyrams · Atnaujinta 2026-03-24 · NCT06430385

Neurophysiologic Biomarkers in Rett Syndrome

  • Children's Hospital of Philadelphia, Philadelphia
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Amžius nuo 1 iki 18 · Moterims · Atnaujinta 2025-10-20 · NCT05932589

Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.