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Thalassemia clinical trials in North Carolina

3 studies for Thalassemia are looking for participants at sites in North Carolina.

Cities in North Carolina

A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia

  • Atrium Levine Children's/Atrium Health, Charlotte
  • Duke University_Durham, Durham
RecruitingPhase 3
Ages 2 and older · All sexes · Updated Sep 18, 2026 · NCT06609226

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Comprehensive Hemophilia Treatment Center, University of North Carolina at Chapel Hill, Chapel Hill
  • St. Jude Affiliate Clinic at Novant Health Hemby Children's Hospital, Charlotte
  • East Carolina University Hemophilia Treatment Center, Greenville
  • and 1 more
RecruitingObservational study
All ages · All sexes · Updated Aug 17, 2026 · NCT04398628

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

  • Levine Children's Hospital - Hematology, Charlotte
RecruitingPhase 3
Ages 12 to 35 · All sexes · Updated Mar 23, 2026 · NCT05477563

From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.