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Achondroplasia clinical trials in California

4 studies for Achondroplasia are looking for participants at sites in California.

Cities in California

A Study of TYRA-300 in Children With Achondroplasia: BEACH301

  • Lundquist Institute for Biomedical Innovation, Torrance
RecruitingPhase 2
Ages 3 to 10 · All sexes · Updated Oct 1, 2026 · NCT06842355

Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia

  • UCSF Benioff Children's Hospital Oakland, Oakland
RecruitingPhase 2/3
Ages 2 to 17 · All sexes · Updated Sep 24, 2026 · NCT07441876

Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH)

  • UCSF Benioff Children's Hospital, Oakland
RecruitingPhase 2
0 Years – 32 Months · All sexes · Updated Jul 13, 2026 · NCT07169279

VIrtual STudy in Achondroplasia for the US (VISTA)

  • UCSF, Oakland
  • PicnicHealth, San Francisco
RecruitingObservational study
0 Months – 18 Years · All sexes · Updated Jun 30, 2026 · NCT06168201

From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.