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Familial Amyloid Neuropathies clinical trials in Pennsylvania
3 studies for Familial Amyloid Neuropathies are looking for participants at sites in Pennsylvania.
Cities in Pennsylvania
Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis
- Research Site, Danville
- Research Site, Philadelphia
- Research Site, Philadelphia
RecruitingObservational study
Ages 18 to 130 · All sexes · Updated Sep 23, 2026 · NCT06465810ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)
- Clinical Trial Site, Philadelphia
RecruitingObservational study
All ages · All sexes · Updated Sep 8, 2026 · NCT04561518Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant
- Penn Presbyterian Medical Center, Philadelphia
- University of Pittsburgh Medical Center, Presbyterian Hospital, Pittsburgh
RecruitingPhase 3
Ages 18 to 75 · All sexes · Updated Aug 4, 2026 · NCT06563895From ClinicalTrials.gov, data retrieved Oct 6, 2026. Each study sets its own eligibility; the study team decides who can join.