Home › Gaucher Disease › Pennsylvania
Gaucher Disease clinical trials in Pennsylvania
5 studies for Gaucher Disease are looking for participants at sites in Pennsylvania.
Cities in Pennsylvania
A Gaucher Disease Gene Therapy Trial With FLT201
- Children's Hospital of Philadelphia, Philadelphia
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RecruitingPhase 3
Ages 18 and older · All sexes · Updated Sep 3, 2026 · NCT07223944International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry
- Penn State Health Milton South Hershey Medical Center- Site Number : 840126, Hershey
- Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
- Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
- and 1 more
RecruitingObservational study
All ages · All sexes · Updated Apr 14, 2026 · NCT00358943Longitudinal Study of Neurodegenerative Disorders
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RecruitingObservational study
All ages · All sexes · Updated Feb 9, 2026 · NCT03333200Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RecruitingObservational study
2 Months – 60 Years · All sexes · Updated Jan 13, 2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RecruitingPhase 2
2 Months – 55 Years · All sexes · Updated Dec 15, 2025 · NCT01962415From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.