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Kajian klinikal Adrenoleukodistrofi di Pennsylvania

4 kajian untuk Adrenoleukodistrofi sedang mencari peserta di lokasi di Pennsylvania.

Bandar di Pennsylvania

Teks kajian rasmi (Bahasa Inggeris)

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaKajian pemerhatian
2 Months – 60 Years · Semua jantina · Dikemas kini 13 Jan 2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaFasa 2
2 Months – 55 Years · Semua jantina · Dikemas kini 15 Dis 2025 · NCT01962415

The Myelin Disorders Biorepository Project

  • The Children's Hospital of Philadelphia, Philadelphia
  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh Medical Center, Pittsburgh
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 23 Okt 2025 · NCT03047369

A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel

  • Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaKajian pemerhatian
Semua umur · Lelaki · Dikemas kini 2 Jul 2025 · NCT06224413

Daripada ClinicalTrials.gov, data diperoleh pada 4 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.