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Kajian klinikal Talasemia Beta di Pennsylvania
5 kajian untuk Talasemia Beta sedang mencari peserta di lokasi di Pennsylvania.
Bandar di Pennsylvania
Teks kajian rasmi (Bahasa Inggeris)
ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia
- Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaFasa 1/2
Umur 18 hingga 40 · Semua jantina · Dikemas kini 23 Sep 2026 · NCT06364774T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias
- Children's Hospital of Pittsburgh of UPMC, Pittsburgh
Mengambil pesertaFasa 1/2
Umur 5 hingga 40 · Semua jantina · Dikemas kini 13 Ogo 2026 · NCT03653338Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaKajian pemerhatian
2 Months – 60 Years · Semua jantina · Dikemas kini 13 Jan 2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaFasa 2
2 Months – 55 Years · Semua jantina · Dikemas kini 15 Dis 2025 · NCT01962415A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel
- Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 11 Feb 2025 · NCT06271512Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.